The U.S. Food and Drug Administration (FDA) has granted Orphan Drug Designation for Arcturus Therapeutics' product candidate ARCT-032 to treat cystic fibrosis (CF).
The FDA’s...
The U.S. Food and Drug Administration has approved Ogsiveo (nirogacestat) tablets for adult patients with progressing desmoid tumors who require systemic treatment. Ogsiveo is...